Biopolym. Cell. 1989; 5(2):5-16.
Дискусії
Задачі і проблеми генної терапії
1Кордюм В. А.
  1. Інститут молекулярної біології і генетики АН УСРС
    Київ, СРСР

Abstract

Здійснено аналіз кола питань, які входять до поняття «генна терапія», у вузькому і широкому визначеннях. З урахуванням складових і вирішуваних нею завдань запропоновано також повне визначення напрямку. У своєму повному значенні генна терапія – це ідентифікація геномів поіндивідуумно, після чого за рахунок корекції спадкового апарату клітин всього організму або окремих тканин усунути молекулярні першооснови уже існуючих у даної людини хвороб і запобігти появі будь-яких нових патологій з часом, а за бажанням (чи за необхідності) впровадити в клітини людини нову генетичну інформації, що забезпечить появу як у тих, хто нині живуть, так і в поколіннях появу потенційно будь-яких фенотипів, аж до взагалі відсутніх у природі.

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