Biopolym. Cell. 1990; 6(2):12-17.
http://dx.doi.org/10.7124/bc.000253
The present and future of the gene therapy of hereditary α1-protease inhibitor deficiency
1Buzhievskaya T. I., 1Chernenko V. Yu., 1Polishchuk L. A.
  1. Institute of Molecular Biology and Genetics, Academy of Sciences of the Ukrainian SSR
    Kiev, USSR

Abstract

Molecular-genetic principles of hereditary α1-protease inhibitor deficiency are reported as well as data concerning the current gene therapy views on this human pathological unit are reviewed.
Full text: (PDF, in Russian)

References

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